BioMed Nexus Industry Directory

Gene & Cell
Therapy Companies

The definitive directory of gene and cell therapy developers, spanning CAR-T and engineered immune cell therapy, CRISPR and next-generation gene editing, AAV gene therapy, rare disease programs, in vivo delivery platforms, and cell & gene manufacturing. Curated for biotech investors, business development leads, and scientists tracking the CGT landscape.

170
Companies Listed
7
Categories
$62B
CGT Market Size (2030)
100,000 Directory Views
65,000+ Newsletter Subscribers
1.1M Monthly Impressions
Distributed via the BioMed Nexus Daily Brief
Directory Gene & Cell Therapy Companies

BioMed Nexus tracks 170 gene and cell therapy companies across 7 categories: CAR-T & immune cell therapy, gene editing & CRISPR, AAV gene therapy, rare disease, in vivo delivery, platform & tools, and autoimmune & other cell therapies. The directory covers the leading CGT developers, including CRISPR Therapeutics, Intellia, Beam, Sarepta, Kite Pharma and Legend Biotech, alongside emerging biotechs. Last updated July 2026

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All Listed Companies / 170 companies

Company Database
BMS (Breyanzi/Abecma)Upgrade listing →
Novartis (Kymriah)Upgrade listing →
Autolus TherapeuticsUpgrade listing →
Allogene TherapeuticsUpgrade listing →
Precision BioSciencesUpgrade listing →
Lyell ImmunopharmaUpgrade listing →
Cartesian TherapeuticsUpgrade listing →
Cabaletta BioUpgrade listing →
Fate TherapeuticsUpgrade listing →
Century TherapeuticsUpgrade listing →
Adicet Bio (Regeneron)Upgrade listing →
Luminary TherapeuticsUpgrade listing →
Iovance BiotherapeuticsUpgrade listing →
Triumvira ImmunologicsUpgrade listing →
Mnemo TherapeuticsUpgrade listing →
Vor BiopharmaUpgrade listing →
Pregene BiopharmaUpgrade listing →
Editas MedicineUpgrade listing →
Prime MedicineUpgrade listing →
Caribou BiosciencesUpgrade listing →
Verve TherapeuticsUpgrade listing →
Tessera TherapeuticsUpgrade listing →
Scribe TherapeuticsUpgrade listing →
Excision BioTherapeuticsUpgrade listing →
Pairwise PlantsUpgrade listing →
Mammoth BiosciencesUpgrade listing →
Arbor BiotechnologiesUpgrade listing →
Aera TherapeuticsUpgrade listing →
Tome BiosciencesUpgrade listing →
Chroma MedicineUpgrade listing →
Tune TherapeuticsUpgrade listing →
Epicrispr BiotechnologiesUpgrade listing →
Locus BiosciencesUpgrade listing →
Poseida Therapeutics (Roche)Upgrade listing →
Sherlock BiosciencesUpgrade listing →
4D Molecular TherapeuticsUpgrade listing →
Adverum BiotechnologiesUpgrade listing →
Akouos (Eli Lilly)Upgrade listing →
Abeona TherapeuticsUpgrade listing →
Freeline TherapeuticsUpgrade listing →
Ultragenyx PharmaceuticalUpgrade listing →
Rocket PharmaceuticalsUpgrade listing →
Prevail Therapeutics (Lilly)Upgrade listing →
Spark Therapeutics (Roche)Upgrade listing →
BioMarin (Roctavian)Upgrade listing →
Voyager TherapeuticsUpgrade listing →
Capsida BiotherapeuticsUpgrade listing →
AAVantgarde BioUpgrade listing →
Affinia TherapeuticsUpgrade listing →
Taysha Gene TherapiesUpgrade listing →
Jaguar Gene TherapyUpgrade listing →
Sangamo TherapeuticsUpgrade listing →
Amicus TherapeuticsUpgrade listing →
BridgeBio PharmaUpgrade listing →
Orchard TherapeuticsUpgrade listing →
Lexeo TherapeuticsUpgrade listing →
Applied DNA SciencesUpgrade listing →
Klotho NeurosciencesUpgrade listing →
Ambys MedicinesUpgrade listing →
Solid BiosciencesUpgrade listing →
Asklepios BioPharmaceuticalUpgrade listing →
Lacerta TherapeuticsUpgrade listing →
Esteve (Gene Therapy)Upgrade listing →
Adrenas TherapeuticsUpgrade listing →
Forge BiologicsUpgrade listing →
Bluerock Therapeutics (Bayer)Upgrade listing →
Novartis Gene Therapies (Zolgensma)Upgrade listing →
Arcturus TherapeuticsUpgrade listing →
Moderna (Gene Therapy)Upgrade listing →
Selecta BiosciencesUpgrade listing →
LogicBio TherapeuticsUpgrade listing →
Generation BioUpgrade listing →
ReCode TherapeuticsUpgrade listing →
Elicio TherapeuticsUpgrade listing →
Genenta ScienceUpgrade listing →
Interius BioTherapeuticsUpgrade listing →
Encoded TherapeuticsUpgrade listing →
Ring TherapeuticsUpgrade listing →
Dyno TherapeuticsUpgrade listing →
Acuitas TherapeuticsUpgrade listing →
Genevant SciencesUpgrade listing →
Omega TherapeuticsUpgrade listing →
Orbital TherapeuticsUpgrade listing →
Sigilon TherapeuticsUpgrade listing →
Oxford BiomedicaUpgrade listing →
Brammer Bio (Thermo Fisher)Upgrade listing →
Center for Breakthrough MedicinesUpgrade listing →
Miltenyi BiotecUpgrade listing →
Lonza Cell & GeneUpgrade listing →
National ResilienceUpgrade listing →
Catalent Cell & GeneUpgrade listing →
WuXi Advanced TherapiesUpgrade listing →
FUJIFILM Cell TherapyUpgrade listing →
Samsung Biologics (CGT)Upgrade listing →
Charles River (CGT)Upgrade listing →
Cytiva (GE Healthcare)Upgrade listing →
Sartorius (CGT Tools)Upgrade listing →
Thermo Fisher Cell TherapyUpgrade listing →
Beckman Coulter (CGT)Upgrade listing →
Bio-Techne (CGT Reagents)Upgrade listing →
ScaleReady (Cytiva/Wilson Wolf)Upgrade listing →
Caladrius BiosciencesUpgrade listing →
Compass TherapeuticsUpgrade listing →
iTeos TherapeuticsUpgrade listing →
Sotio BiotechUpgrade listing →
Adaptimmune (Tecelra)Upgrade listing →
Kyverna TherapeuticsUpgrade listing →
Atara BiotherapeuticsUpgrade listing →
CRISPR TherapeuticsUpgrade listing →
Intellia TherapeuticsUpgrade listing →
Beam TherapeuticsUpgrade listing →
Kite Pharma (Gilead)Upgrade listing →
Legend Biotech / J&JUpgrade listing →
Sarepta TherapeuticsUpgrade listing →
Krystal BiotechUpgrade listing →
Sana BiotechnologyUpgrade listing →
Gracell (AstraZeneca)Upgrade listing →
TScan TherapeuticsUpgrade listing →
Wave Life SciencesUpgrade listing →
Shape TherapeuticsUpgrade listing →
HuidaGene TherapeuticsUpgrade listing →
Kriya TherapeuticsUpgrade listing →
Tenaya TherapeuticsUpgrade listing →
Beacon TherapeuticsUpgrade listing →
Ray TherapeuticsUpgrade listing →
Atsena TherapeuticsUpgrade listing →
Umoja BiopharmaUpgrade listing →
Capstan (AbbVie)Upgrade listing →
Sail BiomedicinesUpgrade listing →
JCR PharmaceuticalsUpgrade listing →
Kyowa Kirin (Orchard)Upgrade listing →
Aldevron (Danaher)Upgrade listing →
Maravai / TriLinkUpgrade listing →
Andelyn BiosciencesUpgrade listing →
Vernal BiosciencesUpgrade listing →

Gene & Cell Therapy Companies: Frequently Asked Questions

How many gene and cell therapy companies are in this directory?
This directory lists 170 gene and cell therapy companies across seven categories: CAR-T and immune cell therapy, gene editing and CRISPR, AAV gene therapy, rare disease, in vivo delivery, platform and tools, and autoimmune and other cell therapies. It is updated regularly by the BioMed Nexus editorial team.
Who are the leading gene and cell therapy companies in 2026?
Leading gene and cell therapy companies include CRISPR Therapeutics, Intellia, Beam Therapeutics, Sarepta, bluebird bio, Krystal Biotech, Kite Pharma (Gilead), Legend Biotech, BioMarin and Ultragenyx. They span CRISPR editing, AAV gene therapy and CAR-T cell therapy.
What are the main types of gene and cell therapy?
Gene and cell therapies include CAR-T and other engineered immune cell therapies, CRISPR and base/prime gene editing, AAV-delivered gene therapy, ex vivo therapies for rare genetic diseases, in vivo delivery via LNP and viral vectors, and emerging autoimmune cell therapies. This directory organizes companies by these seven categories.
What is the difference between gene editing and gene therapy?
Gene therapy typically adds a working copy of a gene using a vector such as AAV, while gene editing (CRISPR, base editing, prime editing) directly modifies the DNA sequence in a patient's cells. Sarepta and REGENXBIO focus on AAV gene therapy, while CRISPR Therapeutics, Intellia and Beam focus on editing.
Which companies make CAR-T cell therapies?
Approved and clinical CAR-T companies include Novartis (Kymriah), BMS (Breyanzi, Abecma), Kite Pharma/Gilead (Yescarta, Tecartus), Legend Biotech/J&J (Carvykti), Autolus, Arcellx and Allogene. Newer firms such as Kyverna and Cabaletta target autoimmune disease with CD19 CAR-T.
How can a company get listed or featured in the directory?
Any gene or cell therapy company can claim a free basic listing. Featured Partners receive priority placement at the top of the directory, a dedicated landing page, backlinks, and a featured segment in the BioMed Nexus daily newsletter reaching 65,000+ subscribers. Spots are limited, so contact the BioMed Nexus partnerships team to learn more.
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About the Gene & Cell Therapy Companies Directory

The BioMed Nexus Gene & Cell Therapy Companies Directory is a comprehensive, regularly updated list of gene and cell therapy developers, spanning CAR-T and engineered immune cell therapy, CRISPR and next-generation gene editing, AAV gene therapy, ex vivo rare disease therapies, in vivo delivery platforms, cell and gene therapy manufacturing (CDMO) and tools, and emerging autoimmune cell therapies. It covers approved-therapy leaders alongside clinical- and preclinical-stage biotechs.

Use it to research gene and cell therapy companies by modality, track the competitive landscape, and map CDMO and platform partners. Whether you are a biotech investor evaluating the CGT sector, a business development lead scouting partners, or a scientist tracking modalities, the directory provides structured, current company data. Curated and maintained by the BioMed Nexus editorial team; last updated July 2026.

Companies can claim a free basic listing or become a Featured Partner for priority placement, a dedicated landing page, backlinks, and a featured segment in the BioMed Nexus daily newsletter reaching 65,000+ subscribers. Contact our partnerships team to learn more.

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